RR Phantom
Location : Wasted Space Job/hobbies : Cayman Islands Actuary
| Subject: Gene therapy on course to claim a first Mon Dec 12, 2011 4:42 am | |
| MEDICAL researchers have successfully treated six patients suffering from the blood-clotting disease known as haemophilia B by injecting them with the correct form of a defective gene.
Haemophilia B is the first well-known disease to appear treatable by gene therapy.
The general concept of gene therapy - replacing the defective gene in any genetic disease with the intact version - has long been alluring.
But carrying it out in practice, usually by loading the replacement gene onto a virus that introduces it into human cells, has been a struggle.
The immune system is all too effective at killing the viruses before the genes can take effect.
The success with haemophilia B, reported online in The New England Journal of Medicine, embodies several minor improvements.
Read more: http://www.smh.com.au/technology/sci-tech/gene-therapy-on-course-to-claim-a-first-20111211-1oprn.html#ixzz1gJP5Cq7J
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